Clinical Study for Treatment-naïve IOPD Babies to Evaluate Efficacy and Safety of ERT With Avalglucosidase Alfa

Trial Identifier: EFC14462
Sponsor: Sanofi
Start Date: September 2021
Primary Completion Date: March 2026
Study Completion Date: August 2027
Condition: Pompe Disease

Available Languages

For questions about your Trial Results Summary, please see Sponsor contact section within your Trial Results Summary.

No documents have been posted yet.

Trial Locations

Country Location
BELGIUM LEUVEN, BELGIUM, 3000
CHINA QINGDAO, CHINA, 266034
CHINA SHANGHAI, CHINA, 200120
GERMANY BAD OEYNHAUSEN, GERMANY, 35392
ITALY, Lombardia MONZA, Lombardia, ITALY, 20052
NETHERLANDS ROTTERDAM, NETHERLANDS, 3015 CE
SPAIN, Catalunya [Cataluña] ESPLUGUES DE LLOBREGAT, Catalunya [Cataluña], SPAIN, 08950
Taiwan TAIPEI CITY, Taiwan, 100
UNITED KINGDOM, London, City of LONDON, London, City of, UNITED KINGDOM, WC1N 3JH
UNITED KINGDOM, Manchester MANCHESTER, Manchester, UNITED KINGDOM, M13 9WL
UNITED STATES, California STANFORD, California, UNITED STATES, 94305
UNITED STATES, Minnesota MINNEAPOLIS, Minnesota, UNITED STATES, 55404
UNITED STATES, New York HAWTHORNE, New York, UNITED STATES, 10532
UNITED STATES, North Carolina DURHAM, North Carolina, UNITED STATES, 27710
UNITED STATES, Ohio CINCINNATI, Ohio, UNITED STATES, 45229
UNITED STATES, Washington SEATTLE, Washington, UNITED STATES, 98105